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Pierpaolo Ala Selected Research

Pierpaolo Ala Research Topics

Disease

5Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker)
01/2023 - 01/2020
5Muscular Dystrophies (Muscular Dystrophy)
01/2022 - 09/2017
1Neuromuscular Diseases (Neuromuscular Disease)
01/2023
1Atrophy
01/2022
1Muscle Weakness
01/2022
1Congenital Disorders of Glycosylation
01/2022
1Disease Progression
01/2020
1Limb-Girdle Muscular Dystrophies (Limb-Girdle Muscular Dystrophy)
01/2018
1Scleroatonic muscular dystrophy
09/2017

Drug/Important Bio-Agent (IBA)

3DystrophinIBA
01/2023 - 01/2020
3Proteins (Proteins, Gene)FDA Link
01/2023 - 09/2017
3Dystroglycans (Dystroglycan)IBA
01/2022 - 01/2018
2Biomarkers (Surrogate Marker)IBA
11/2020 - 01/2020
2CollagenIBA
09/2020 - 09/2017
1Messenger RNA (mRNA)IBA
01/2023
1Protein Isoforms (Isoforms)IBA
01/2023
1Congenital disorder of glycosylation type 1AIBA
01/2022
1Creatine Kinase (Creatine Phosphokinase)IBA
01/2022
1MicroRNAs (MicroRNA)IBA
11/2020
1Blood Proteins (Serum Proteins)IBA
01/2020
1Laminin (Merosin)IBA
11/2019
1Collagen Type VIIBA
09/2017
1Antisense OligonucleotidesIBA
09/2017

Therapy/Procedure

1Therapeutics
01/2023